Golodirsen

Sold as VYONDYS 53 · given by intravenous

One to three years until it comes off patent
1.9 yr
Until anyone may copy it
Protection runs to 2028-06-28
1
Trials running now
6 registered in total
In routine use
Furthest stage reached
already in routine clinical use
3
Organisations running trials
lead sponsors on record
01

Who owns it, and until when

Sarepta Therapeutics Inc
Approval holder
the only company permitted to sell it today
2028-06
Last patent expires
latest patent filed against this product
2026-12
FDA exclusivity ends
a separate protection granted at approval

Whichever date falls later is when other manufacturers may apply to sell copies. Price typically falls steeply within a year of that point, and with it any company's ability to recover the cost of new research on the molecule. That is when it becomes a candidate for the ledger on the first tab.

02

What it is being tested for

Duchenne Muscular Dystrophy
03

Who is paying for the research

Sarepta Therapeutics, Inc.
Company
4
Kevin Flanigan
University or hospital
1
Rare Disease Research, LLC
University or hospital
1

Who funds the trials matters after protection lapses. Company-funded work usually stops once exclusivity ends; university, hospital and government-funded work does not, and is the research most likely to continue on this molecule afterwards.

04

The trials themselves

NCT04708314In routine use2020 · 2 people · stopped early
An Open-Label Study of Golodirsen in Non-Amb

Expiry dates are what the patent holder has filed; litigation, paediatric extensions and settlements routinely move them, so read these as the earliest plausible date rather than a schedule. Not medical advice.

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